New Compassionate Allowance Conditions (effective March 1, 2010) |
1 |
Alstrom Syndrome |
2 |
Amegakaryocytic Thrombocytopenia |
3 |
Ataxia Spinocerebellar |
4 |
Ataxia Telangiectasia |
5 |
Batten Disease |
6 |
Bilateral Retinoblastoma |
7 |
Cri du Chat Syndrome |
8 |
Degos Disease |
9 |
Early-Onset Alzheimer’s Disease |
10 |
Edwards Syndrome |
11 |
Fibrodysplasia Ossificans Progressiva |
12 |
Fukuyama Congenital Muscular Dystrophy |
13 |
Glutaric Acidemia Type II |
14 |
Hemophagocytic Lymphohistiocytosis (HLH), Familial Type |
15 |
Hurler Syndrome, Type IH |
16 |
Hunter Syndrome, Type II |
17 |
Idiopathic Pulmonary Fibrosis |
18 |
Junctional Epidermolysis Bullosa, Lethal Type |
19 |
Late Infantile Neuronal Ceroid Lipofuscinoses |
20 |
Leigh’s Disease |
21 |
Maple Syrup Urine Disease |
22 |
Merosin Deficient Congenital Muscular Dystrophy |
23 |
Mixed Dementia |
24 |
Mucosal Malignant Melanoma |
25 |
Neonatal Adrenoleukodystrophy |
26 |
Neuronal Ceroid Lipofuscinoses, Infantile Type |
27 |
Niemann-Pick Type C |
28 |
Patau Syndrome |
29 |
Primary Progressive Aphasia |
30 |
Progressive Multifocal Leukoencephalopathy |
31 |
Sanfilippo Syndrome |
32 |
Subacute Sclerosis Panencephalitis |
33 |
Tay Sachs Disease |
34 |
Thanatophoric Dysplasia, Type 1 |
35 |
Ullrich Congenital Muscular Dystrophy |
36 |
Walker Warburg Syndrome |
37 |
Wolman Disease |
38 |
Zellweger Syndrome |